Dystrophy Clinical Trials

Find clinical trials for Dystrophy. Search for Dystrophy clinical trials in different cities and states across the United States.

Dystrophy

e.g. Massachusetts•Healthy volunteers: No

Filter results

Results: 114

A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia

Recruiting

Phase 1

Phase 2

Sponsor:

Benitec Biopharma, Inc.

Location:

New York

Code:

NCT06185673

Conditions

Oculopharyngeal Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 0 - 65

Healthy Volunteers: Not accepted

Interventions

BB-301: Dose escalation phase 1b cohort 1

BB-301: Dose escalation phase 1b cohort 2

BB-301: Dose escalation phase 1b cohort 3

BB-301: Dose expansion phase 2a

Twice Weekly Steroids and Exercise as Therapy for DMD

Recruiting

Phase 2

Sponsor:

University of Florida

Location:

Gainesville

Code:

NCT04322357

Conditions

Duchenne Muscular Dystrophy (DMD)

Eligibility Criteria

Sex: Male

Age: 5 - 9

Healthy Volunteers: Not accepted

Interventions

Prednisone

In-home Exercise Training

Prednisone plus exercise

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy.

Recruiting

Sponsor:

Catalyst Pharmaceuticals, Inc.

Location:

Little Rock, North Worcester, Denton

Code:

NCT06564974

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 2+

Healthy Volunteers: Not accepted

Interventions

Vamorolone

Optical Coherence Tomography Guided Transepithelial Phototherapeutic Keratectomy

Recruiting

Sponsor:

Oregon Health and Science University

Location:

Portland

Code:

NCT01243931

Conditions

Corneal Opacity

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

OCT-guided laser phototherapeutic keratectomy

Defining Endpoints in Becker Muscular Dystrophy

Recruiting

Sponsor:

Virginia Commonwealth University

Location:

Orange, Aurora, Iowa City, Kansas Cityshow 5 more

Code:

NCT05257473

Conditions

Becker Muscular Dystrophy

Muscular Dystrophies

Muscular Dystrophy in Children

Muscular Dystrophy, Becker

Eligibility Criteria

Sex: Male

Age: 6+

Healthy Volunteers: Not accepted

Motor Outcomes to Validate Evaluations in FSHD (MOVE FSHD)

Recruiting

Sponsor:

University of Kansas Medical Center

Location:

Los Angeles, Stanford, Aurora, Gainesvilleshow 9 more

Code:

NCT04635891

Conditions

FSHD

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

Oral N-acetylcysteine for Retinitis Pigmentosa

Recruiting

Phase 3

Sponsor:

Johns Hopkins University

Location:

Davis, Los Angeles, San Francisco, Stanfordshow 19 more

Code:

NCT05537220

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18 - 65

Healthy Volunteers: Not accepted

Interventions

N-acetylcysteine

Placebo

Nomad P-KAFO Study

Recruiting

Sponsor:

Shirley Ryan AbilityLab

Location:

Chicago

Code:

NCT05644522

Conditions

Cerebrovascular Accident

Post-polio Syndrome

Spinal Cord Injuries

Multiple Sclerosis

Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 18 - 70+

Healthy Volunteers: Not accepted

Interventions

Indego Nomad® Powered Knee-Ankle-Foot Orthosis (P-KAFO) (Parker Hannifin Corp., Cleveland, OH)

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

Recruiting

Phase 1

Phase 2

Sponsor:

Solid Biosciences Inc.

Location:

Los Angeles, Columbus

Code:

NCT06138639

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 4 - 7

Healthy Volunteers: Not accepted

Interventions

SGT-003

Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I)

Recruiting

Phase 3

Sponsor:

ML Bio Solutions, Inc.

Location:

Little Rock, Irvine, Aurora, Gainesvilleshow 11 more

Code:

NCT05775848

Conditions

Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I)

Eligibility Criteria

Sex: All

Age: 12 - 60

Healthy Volunteers: Not accepted

Interventions

BBP-418 (ribitol)

Placebo

Dystrophy

e.g. Massachusetts•Healthy volunteers: No

Filter results

Results: 114

A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia

Recruiting

Phase 1

Phase 2

Sponsor:

Benitec Biopharma, Inc.

Location:

New York

Code:

NCT06185673

Conditions

Oculopharyngeal Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 0 - 65

Healthy Volunteers: Not accepted

Interventions

BB-301: Dose escalation phase 1b cohort 1

BB-301: Dose escalation phase 1b cohort 2

BB-301: Dose escalation phase 1b cohort 3

BB-301: Dose expansion phase 2a

Twice Weekly Steroids and Exercise as Therapy for DMD

Recruiting

Phase 2

Sponsor:

University of Florida

Location:

Gainesville

Code:

NCT04322357

Conditions

Duchenne Muscular Dystrophy (DMD)

Eligibility Criteria

Sex: Male

Age: 5 - 9

Healthy Volunteers: Not accepted

Interventions

Prednisone

In-home Exercise Training

Prednisone plus exercise

Registry Study to Observe Long-term Safety of Vamorolone (AGAMREE®) in Patients With Duchenne Muscular Dystrophy.

Recruiting

Sponsor:

Catalyst Pharmaceuticals, Inc.

Location:

Little Rock, North Worcester, Denton

Code:

NCT06564974

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 2+

Healthy Volunteers: Not accepted

Interventions

Vamorolone

Optical Coherence Tomography Guided Transepithelial Phototherapeutic Keratectomy

Recruiting

Sponsor:

Oregon Health and Science University

Location:

Portland

Code:

NCT01243931

Conditions

Corneal Opacity

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

OCT-guided laser phototherapeutic keratectomy

Defining Endpoints in Becker Muscular Dystrophy

Recruiting

Sponsor:

Virginia Commonwealth University

Location:

Orange, Aurora, Iowa City, Kansas Cityshow 5 more

Code:

NCT05257473

Conditions

Becker Muscular Dystrophy

Muscular Dystrophies

Muscular Dystrophy in Children

Muscular Dystrophy, Becker

Eligibility Criteria

Sex: Male

Age: 6+

Healthy Volunteers: Not accepted

Motor Outcomes to Validate Evaluations in FSHD (MOVE FSHD)

Recruiting

Sponsor:

University of Kansas Medical Center

Location:

Los Angeles, Stanford, Aurora, Gainesvilleshow 9 more

Code:

NCT04635891

Conditions

FSHD

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

Oral N-acetylcysteine for Retinitis Pigmentosa

Recruiting

Phase 3

Sponsor:

Johns Hopkins University

Location:

Davis, Los Angeles, San Francisco, Stanfordshow 19 more

Code:

NCT05537220

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18 - 65

Healthy Volunteers: Not accepted

Interventions

N-acetylcysteine

Placebo

Nomad P-KAFO Study

Recruiting

Sponsor:

Shirley Ryan AbilityLab

Location:

Chicago

Code:

NCT05644522

Conditions

Cerebrovascular Accident

Post-polio Syndrome

Spinal Cord Injuries

Multiple Sclerosis

Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 18 - 70+

Healthy Volunteers: Not accepted

Interventions

Indego Nomad® Powered Knee-Ankle-Foot Orthosis (P-KAFO) (Parker Hannifin Corp., Cleveland, OH)

A Study of SGT-003 Gene Therapy in Duchenne Muscular Dystrophy (INSPIRE DUCHENNE)

Recruiting

Phase 1

Phase 2

Sponsor:

Solid Biosciences Inc.

Location:

Los Angeles, Columbus

Code:

NCT06138639

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 4 - 7

Healthy Volunteers: Not accepted

Interventions

SGT-003

Study to Evaluate the Efficacy and Safety of BBP-418 (Ribitol) in Patients With Limb Girdle Muscular Dystrophy 2I (LGMD2I)

Recruiting

Phase 3

Sponsor:

ML Bio Solutions, Inc.

Location:

Little Rock, Irvine, Aurora, Gainesvilleshow 11 more

Code:

NCT05775848

Conditions

Limb-Girdle Muscular Dystrophy Type 2I (LGMD2I)

Eligibility Criteria

Sex: All

Age: 12 - 60

Healthy Volunteers: Not accepted

Interventions

BBP-418 (ribitol)

Placebo