Dystrophy Clinical Trials

Find clinical trials for Dystrophy. Search for Dystrophy clinical trials in different cities and states across the United States.

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Results: 120

Observational StudyLGMD R1 Natural History Study

Recruiting

Sponsor:

Virginia Commonwealth University

Location:

Orange CA, Aurora CO, Gainesville FL, Shipshewana INshow 6 more

Code:

NCT05618080

Conditions

Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A

Limb Girdle Muscular Dystrophy

Limb Girdle Muscular Dystrophy Type R1

LGMD2A

Eligibility Criteria

Sex: All

Age: 12 - 50

Healthy Volunteers: Not accepted

VP-001MAD of IVT VP-001 in PRPF31 Mutation-Associated Retinal Dystrophy Subjects (Wallaby)

Recruiting

PHASE1

Sponsor:

PYC Therapeutics

Location:

Jacksonville FL, Ann Arbor MI, Portland OR, Dallas TXshow 1 more

Code:

NCT06455826

Conditions

Retinitis Pigmentosa 11

Retinal Degeneration

Eye Diseases

Retinal Disease

Retinal Dystrophies

Eligibility Criteria

Sex: All

Age: 12+

Healthy Volunteers: Not accepted

Interventions

VP-001

Cell Based TherapyTrial of Cell Based Therapy for DMD

Recruiting

PHASE1

Sponsor:

Masonic Cancer Center, University of Minnesota

Location:

Minneapolis MN

Code:

NCT06692426

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

MyoPAXon

Tacrolimus

MSO EvaluationMotor Outcomes to Validate Evaluations in FSHD (MOVE FSHD)

Recruiting

Sponsor:

University of Kansas Medical Center

Location:

Los Angeles CA, Stanford CA, Aurora CO, Gainesville FLshow 14 more

Code:

NCT04635891

Conditions

FSHD

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

GeneticsGenetics of Cardiovascular and Neuromuscular Disease

Recruiting

Sponsor:

University of Chicago

Location:

Chicago IL

Code:

NCT00138931

Conditions

Cardiomyopathy

Arrhythmia

Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 0 - 70+

Healthy Volunteers: Not accepted

Interventions

Blood draw (genetic testing)

OCT Guided PTKOptical Coherence Tomography Guided Transepithelial Phototherapeutic Keratectomy

Recruiting

Sponsor:

Oregon Health and Science University

Location:

Portland OR

Code:

NCT01243931

Conditions

Corneal Opacity

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

OCT-guided laser phototherapeutic keratectomy

Observational StudyA Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years of Age, Who Are Managed in Routine Clinical Practice

Recruiting

Sponsor:

Sarepta Therapeutics, Inc.

Location:

Phoenix AZ, Little Rock AR, La Jolla CA, Sacramento CAshow 8 more

Code:

NCT04475926

Conditions

Limb-girdle Muscular Dystrophy

Eligibility Criteria

Sex: All

Age: 4+

Healthy Volunteers: Not accepted

INS1201A Study to Investigate the Safety and Biodistribution of a Single Intrathecal (IT) Injection of INS1201 in Ambulatory Males With Duchenne Muscular Dystrophy (DMD)

Recruiting

PHASE1

Sponsor:

Insmed Gene Therapy LLC

Location:

Atlanta GA

Code:

NCT06817382

Conditions

Duchenne Muscular Dystrophy

Eligibility Criteria

Sex: Male

Age: 2 - 4

Healthy Volunteers: Not accepted

Interventions

INS1201

N-acetylcysteineOral N-acetylcysteine for Retinitis Pigmentosa

Recruiting

PHASE3

Sponsor:

Johns Hopkins University

Location:

Davis CA, Los Angeles CA, San Francisco CA, Stanford CAshow 21 more

Code:

NCT05537220

Conditions

Retinitis Pigmentosa

Eligibility Criteria

Sex: All

Age: 18 - 65

Healthy Volunteers: Not accepted

Interventions

N-acetylcysteine

Placebo

SERCA2aModulation of SERCA2a of Intra-Myocytic Calcium Trafficking in Cardiomyopathy Secondary to Duchenne Muscular Dystrophy

Recruiting

PHASE1

Sponsor:

Sardocor Corp.

Location:

Kansas City KS, Cincinnati OH, Columbus OH

Code:

NCT06224660

Conditions

DMD-Associated Dilated Cardiomyopathy

Eligibility Criteria

Sex: Male

Age: 18+

Healthy Volunteers: Not accepted

Interventions

SRD-001