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Dystrophy Clinical Trials

Find clinical trials for Dystrophy. Search for Dystrophy clinical trials in different cities and states across the United States.

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Motor Outcomes to Validate Evaluations in Pediatric FSHD (MOVE Peds)

for
Muscular Dystrophy, Facioscapulohumeral
Location: Rochester NY, Durham NC, Kansas City KS
Sponsor: University of Kansas Medical Center

Sex: All

Age: 5 - 17

Code: NCT06847282

Recruiting
Active & Responsive

Wearable Technology to Evaluate Hyperglycemia and HRV in DMD

for
Duchenne Muscular Dystrophy
Location: Nashville TN
Sponsor: Vanderbilt University Medical Center

Sex: Male

Age: 10+

Code: NCT06124196

Recruiting
Active & Responsive

LGMD R1 Natural History Study

for
Calpain-3 Deficiency Limb Girdle Muscular Dystrophy Type 2A,
Location: Richmond VA, Columbus OH, Shipshewana IN, St Louis MO,
Sponsor: Virginia Commonwealth University

Sex: All

Age: 12 - 50

Code: NCT05618080

Recruiting
Active & Responsive

Observation Study in Patients Age 0-5 Years With LAMA2-related Congenital Muscular Dystrophy

for
LAMA2-MD \(Merosin Deficient Congenital Muscular Dystrophy, MDC1A\),
Location: Boston MA, Rochester NY, Columbus OH, Cincinnati OH,
Sponsor: Nationwide Children's Hospital

Sex: All

Age: 0 - 5

Code: NCT06503367

Recruiting
Active & Responsive

DMCRN-02-001: Assessing Pediatric Endpoints in DM1

for
Congenital Myotonic Dystrophy, CDM
Location: Richmond VA, Rochester NY, Fairway KS, Los Angeles CA
Sponsor: Virginia Commonwealth University

Sex: All

Age: 0 - 4

Code: NCT05224778

Recruiting

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Active & Responsive

AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Males With DMD

for
Duchenne Muscular Dystrophy
Location: Atlanta GA
Sponsor: REGENXBIO Inc.

Sex: Male

Age: 0 - 25

Code: NCT05683379

Recruiting
Active & Responsive

Trial of Cell Based Therapy for DMD

for
Duchenne Muscular Dystrophy
Location: Minneapolis MN
Sponsor: Masonic Cancer Center, University of Minnesota

Sex: All

Age: 18+

Code: NCT06692426

Phase1, Recruiting
Active & Responsive

Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders

for
Spinal Muscular Atrophy Type 3,
Location: Boston MA, New York NY, Palo Alto CA
Sponsor: Columbia University

Sex: All

Age: 5+

Code: NCT06839469

Recruiting
Active & Responsive

A Study of SGT-003 Gene Therapy in Ambulant Males With Duchenne Muscular Dystrophy (IMPACT DUCHENNE)

for
Duchenne Muscular Dystrophy
Location: Vancouver
Sponsor: Solid Biosciences Inc.

Sex: Male

Age: 7 - 11

Code: NCT07160634

Phase3, Recruiting
Active & Responsive

An Open-Label Extension Study of PGN-EDODM1 in People With Myotonic Dystrophy Type 1 (FREEDOM-OLE)

for
Myotonic Dystrophy 1
Location: Saguenay, Ottawa
Sponsor: PepGen Inc

Sex: All

Age: 0+

Code: NCT07220603

Phase2, Recruiting