Sponsor:
Paul Szabolcs
Code:
NCT01962415
Conditions
Primary Immunodeficiency (PID)
Congenital Bone Marrow Failure Syndromes
Inherited Metabolic Disorders (IMD)
Hereditary Anemias
Inflammatory Conditions
Eligibility Criteria
Sex: All
Age: 2 - 55
Healthy Volunteers: Not accepted
Interventions
Hydroxyurea
Alemtuzumab
Fludarabine
Melphalan
Thiotepa
Study Details
Eligibility Criteria
Study Design
Interventions and Outcome Measures
Central Contacts and Locations
More Information
Trial information was received from ClinicalTrials.gov and was last updated on 2025-06-16. This information was provided to ClinicalTrials.gov by Paul Szabolcs on 2025-03-18.