UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Recruiting

Phase 1

UCB TransplantUCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells

Sponsor:

Joanne Kurtzberg, MD

Code:

NCT02254863

Conditions

Adrenoleukodystrophy

Batten Disease

Mucopolysaccharidosis II

Leukodystrophy, Globoid Cell

Leukodystrophy, Metachromatic

Eligibility Criteria

Sex: All

Age: 0 - 22

Healthy Volunteers: Not accepted

Interventions

DUOC-01

Study Details

Eligibility Criteria

Study Design

Interventions and Outcome Measures

Central Contacts and Locations

More Information

Trial information was received from ClinicalTrials.gov and was last updated on 2025-11-09. This information was provided to ClinicalTrials.gov by Joanne Kurtzberg, MD on 2025-09-08.