Recruiting

Observational Study

Sponsor:

Immune Oncology Research Institute

Code:

NCT05430971

Conditions

Blastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN)

Eligibility Criteria

Sex: All

Age: 0+

Healthy Volunteers: Not accepted

Study Details

Brief summary:

Blastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN) is a very rare hematologic malignancy. Despite recent advances, at present there is no consensus on the optimal treatment of BPDCN. The optimal therapy of disease remains to be determined, and due to the rarity of cases, there is a need for international collaboration to collect data on BPDCN clinical presentations, diagnostics, treatment regimens and outcomes. Therefore, the objectives of this study are: (1) to build a large database of patients with BPDCN, (2) to investigate the characteristics and outcome of the disease with different treatment regimens, (3) to evaluate prognostic factors, and (4) to generate data-based prospective treatment recommendations.

Conditions

Blastic Plasmacytoid Dendritic Cell Neoplasm (BPDCN)

Study ID

NCT05430971

Start date

Jul 1, 2022

Status verified date

Feb, 2026

Completion date

Jul, 2032

Anticipated

Primary completion date

Jul, 2032

Anticipated

Eligibility Criteria

Eligibility Criteria

Sex: All

Age: 0+

Healthy Volunteers: Not accepted

Inclusion Criteria:

  • Diagnosis of BPDCN
  • Signed informed consent form for prospective patients

Exclusion Criteria:

\-

Study Design

Enrollment

200 participants

Anticipated

Interventions and Outcome Measures

Primary outcome measure

  • Overall survival [ Time Frame: 5 years ]

Central Contacts and Locations

Locations

Sylvester Comprehensive Cancer Center, University of Miami

Recruiting

Miami, Florida, United States, 33136

Contacts

Dickran Kazandjian, MD

dkazandjian@miami.edu

Alvaro Alencar, MD

aalencar@med.miami.edu

Moffitt Cancer Center

Recruiting

Tampa, Florida, United States, 33612

Contacts

Rami Komrokji, MD

rami.komrokji@moffitt.org

Seattle Children's Cancer and Blood Disorders Center

Recruiting

Seattle, Washington, United States, 98145

Contacts

University of Calgary

Recruiting

Calgary, Alberta, Canada, T2N 1N4

Contacts

Carolyn Owen, MD

carolyn.owen@ahs.ca

Children's Hospital of Eastern Ontario, University of Ottawa

Recruiting

Ottawa, Ontario, Canada, K1H 8L1

Contacts

Consolato Sergi, MD, PhD

csergi@cheo.on.ca

More Information

Sponsor

Immune Oncology Research Institute

Last update posted

Jun 5, 2026

Last verified

Feb, 2026

Trial information was received from ClinicalTrials.gov and was last updated on 2026-09-08. This information was provided to ClinicalTrials.gov by Immune Oncology Research Institute on 2026-06-05.