Recruiting
Phase 2

IP-001

Sponsor:

Robert C. Martin

Code:

NCT06526338

Conditions

Hepatocellular Carcinoma

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Interventions

1.0% IP-001 for injection

Surgical Resection and Local Ablation

Local Ablation Alone

Study Details

Brief summary:

The purpose of this study is to evaluate the safety and efficacy of administration of intratumoral IP-001 injection at different dosages (volume and concentration) following local microwave ablation (MWA) or surgical resection and ablation in patients with hepatocellular carcinoma (HCC).

Conditions

Hepatocellular Carcinoma

Study ID

NCT06526338

Start date

Jul 24, 2024

Status verified date

Sep, 2026

Completion date

Dec, 2030

Anticipated

Primary completion date

Dec, 2029

Anticipated

Eligibility Criteria

Eligibility Criteria

Sex: All

Age: 18+

Healthy Volunteers: Not accepted

Inclusion Criteria:

  • Age ≥ 18 years at time of signing Informed Consent.
  • Has a diagnosis of hepatocellular carcinoma (HCC) documented radiologically by American Association for the Study of Liver Diseases (AASLD) criteria and/or histopathologically from a tumor biopsy.
  • Has a treatment plan to receive a curative ablation (MWA only) or a curative surgical resection and ablation, or where the patient may benefit from surgery and ablation or ablation prior to receiving anti-cancer therapy.
  • Has HCC with intermediate, high or very high risk of recurrence.
  • Has hepatic only HCC (disease confined to the liver only), defined by no extra-hepatic lesions greater than 1 cm in size.
  • Has an Eastern Cooperative Oncology Group (ECOG) performance status of 0-1.
  • Patient with past or ongoing hepatitis C virus (HCV) infection will be eligible if the patient has completed HCV treatment at least 1 month prior to Day 1.
  • Patient with controlled hepatitis B will be eligible if the patient meets the following criteria:

1. Antiviral therapy for hepatitis B virus (HBV) must be given for at least 4 weeks, and HBV viral load must be less than 500 IU/mL prior to treatment. Patients on active HBV therapy with viral loads under 500 IU/mL should stay on the same therapy throughout study treatment.
2. Patients who are hepatitis B core antibody (anti-HBc) positive, negative for HBsAg, and negative or positive for anti- HBs, and who have an HBV viral load under 500 IU/mL do not require HBV anti-viral prophylaxis.
  • Patients who are not exposed to unreasonable risks by continued use of the investigational agent in spite of progression of disease. Such criteria may include the following:

1. Absence of symptoms and signs indicating clinically significant progression of disease.
2. No decline in performance status, as measured by ECOG or Karnofsky or both.
3. Absence of symptomatic rapid disease progression requiring urgent medical intervention.
4. Ensure that patients are reconsenting to treatment with the Informed Consent clearly stating that retreatment is not standard of care.
  • Has adequate organ function as specified in the Adequate Organ Function Laboratory Values Table. Specimens must be collected within 14 days prior to Day 1.

1. Hematological: Absolute neutrophil count ≥1500/µL or ANC of ≤1500/µL if there is a stable medical history of neutropenia per provider discretion; Platelets ≥40,000/µL; Hemoglobin ≥8.0 g/dL.
2. Renal: Creatinine OR measured or calculated creatinine clearance (GFR can also be used in place of creatinine or CrCl) ≤1.5 × ULN OR GFR ≥30 mL/min for patients with creatinine levels >1.5 × institutional ULN
3. Hepatic: Total bilirubin ≤2 mg/dL OR direct bilirubin ≤ULN for patients with total bilirubin levels >2 mg/dL; AST (SGOT) and ALT (SGPT) ≤5 × ULN; Albumin (c) >2.6 g/dL
4. Coagulation: International normalized ratio (INR) OR prothrombin time (PT) ≤1.5 × ULN unless patient is receiving anticoagulant therapy as long as PT is within therapeutic range of intended use of anticoagulants

Retreatment Inclusion Criteria:

  • Patients receiving retreatment with IP-001 following intrahepatic recurrence must satisfy all of the following:
  • Radiographic recurrence remains amenable to curative-intent thermal ablation.
  • No symptomatic rapid disease progression requiring urgent systemic therapy or palliative intervention.
  • ECOG performance status remains 0-2.
  • No evidence of clinically significant hepatic decompensation.
  • No extrahepatic disease that would preclude additional local therapy.
  • The Investigator determines that additional thermal ablation remains clinically appropriate.
  • The patient continues to satisfy protocol safety requirements.

Exclusion Criteria:

  • Known allergic reaction to shellfish, crabs, crustacean, or any trial components used in trial treatment.
  • Has an active infection requiring systemic therapy.
  • Has a diagnosis of immunodeficiency or currently receiving chronic systemic steroid therapy (in dosing exceeding 10 mg daily of prednisone equivalent), or any other form of immunosuppressive therapy within 7 days prior to treatment day (Day 1), or has plans to start treatment including >10 mg daily of prednisone equivalent or any immunotherapy.
  • Has an active autoimmune disease that has required systemic treatment in the past 2 years (i.e., with use of disease modifying agents or immunosuppressive drugs). NOTE: replacement therapy (e.g., thyroxine or insulin) is not considered a form of systemic treatment and is allowed.
  • Has had an allogeneic tissue/solid organ transplant, or eligible for a liver transplant and/or on the liver transplantation waiting list.
  • History of idiopathic pulmonary fibrosis, organizing pneumonia (e.g., bronchiolitis obliterans), drug-induced pneumonitis, active tuberculosis, or idiopathic pneumonitis.
  • Has received local therapy to the liver, ablation other than microwave ablation (i.e., alcohol ablation, transcatheter chemoembolization, transcatheter embolization, hepatic arterial infusion, local radiation/Stereotactic Body Radiation Therapy or radioembolization) less than 3 months prior to treatment.
  • Is receiving any of the following prohibited concomitant therapies less than 21 days from treatment or 5 drug elimination half-lives, whichever is shorter, prior to randomization:

1. Antineoplastic systemic chemotherapy or biological therapy.
2. Immunotherapy not specified in this protocol.
3. Systemic glucocorticoids for any purpose other than to modulate symptoms from an adverse event (AE) that is suspected to have an immunologic etiology. Inhaled or topical steroids are allowed, and systemic steroids at doses ≤10 mg/day prednisone or equivalent are allowed. Exception: steroids may be used for premedication prior to imaging.
  • Has received a live vaccine within 28 days prior to treatment Day 1.

Retreatment Exclusion Criteria:

  • Development of symptomatic extrahepatic disease.
  • ECOG >2 attributable to cancer progression.
  • Rapid multifocal progression requiring systemic therapy.
  • Investigator determination that further local therapy is unlikely to provide meaningful clinical benefit.
  • Withdrawal of consent.

Study Design

Enrollment

315 participants

Anticipated

Allocation

Randomized

Intervention Model

Parallel Assignment

Primary purpose

Treatment

Interventions and Outcome Measures

Arms

experimental: Arm A: Participants with ≤3 hepatic tumors that can be treated in one ablation session

Participants will be randomized 1:1:1 to receive intratumoral injection of IP-001 (10 mg/mL, 4 mL \[low volume\]) immediately following local microwave ablation or surgical resection and local microwave ablation

active comparator: Arm B: Participants with ≤3 hepatic tumors that can be treated in one ablation session

Participants will be randomized 1:1:1 to receive local microwave ablation or surgical resection and local microwave ablation alone

experimental: Arm C: Participants with ≤3 hepatic tumors that can be treated in one ablation session

Participants will be randomized 1:1:1 to receive intratumoral injection of IP-001 (10 mg/mL, up to 12 mL \[high volume\]) immediately following local microwave ablation or surgical resection and local microwave ablation

experimental: Arm D: Participants with >3 hepatic tumors that can be treated in more than one ablation session

Participants will be randomized 1:1 to receive intratumoral injection of IP-001 (10mg/mL \[high concentration\], up to 12 mL) immediately following local microwave ablation or surgical resection and local microwave ablation

experimental: Arm E: Participants with >3 hepatic tumors that can be treated in more than one ablation session

Participants will be randomized 1:1 to receive intratumoral injection of diluted IP-001 (1 mg/mL \[low concentration\], up to 12 mL) immediately following local microwave ablation or surgical resection and local microwave ablation

Interventions

1.0% IP-001 for injection

Participants will receive intratumoral injection of 1.0% IP-001 following local microwave ablation or surgical resection and local microwave ablation

Surgical Resection and Local Ablation

Participants will undergo surgical resection of the tumor and local microwave ablation

Local Ablation Alone

Participants will have local ablation of the tumor by microwave ablation alone

Primary outcome measure

  • Recurrence Free Survival [ Time Frame: From Date of Randomization until date of documented progression, assessed up to 60 months ]

Central Contacts and Locations

Central contacts

Locations

University of Louisville

Recruiting

Louisville, Kentucky, United States, 40202

Contacts

Principal Investigator:

Robert Martin, MD, PhD

More Information

Sponsor

Robert C. Martin

Last update posted

Sep 4, 2026

Last verified

Sep, 2026

Trial information was received from ClinicalTrials.gov and was last updated on 2026-09-10. This information was provided to ClinicalTrials.gov by Robert C. Martin on 2026-09-04.