Exploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies

Recruiting

SMN-Directed TherapiesExploring the Physiologic, Pharmacodynamic, and Clinical Responses of Skeletal Muscle in Patients With Spinal Muscular Atrophy Treated With SMN-Directed Therapies

Sponsor:

St. Jude Children's Research Hospital

Code:

NCT06532474

Conditions

Spinal Muscular Atrophy

Eligibility Criteria

Sex: All

Age: 5 - 20

Healthy Volunteers: Not accepted

Study Details

Eligibility Criteria

Study Design

Interventions and Outcome Measures

Central Contacts and Locations

More Information

Trial information was received from ClinicalTrials.gov and was last updated on 2026-01-08. This information was provided to ClinicalTrials.gov by St. Jude Children's Research Hospital on 2025-11-04.