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Dystrophy Clinical Trials

Browse 493 Dystrophy clinical trials enrolling across the United States and Canada. Search by city or state to find one near you.

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Feasibility of the BrainGate2 Neural Interface System in Persons With Tetraplegia

for
Anarthria, Dysarthria, Tetraplegia, Spinal Cord Injuries,
Location: Boston MA, Stanford CA
Sponsor: Leigh R. Hochberg, MD, PhD.

Sex: All

Age: 18 - 70+

Code: NCT05724173

Recruiting

Evaluating Long-term Use of a Pediatric Robotic Exoskeleton (P.REX/Agilik) to Improve Gait in Children With Movement Disorders

for
Cerebral Palsy, Muscular Dystrophy, Spina Bifida,
Location: Bethesda MD
Sponsor: National Institutes of Health Clinical Center (CC)

Sex: All

Age: 3 - 17

Code: NCT05726591

Recruiting

A Study to Evaluate the Safety and Clinical Activity of Intramuscular Doses of BB-301 Administered to Subjects With Oculopharyngeal Muscular Dystrophy With Dysphagia

for
Oculopharyngeal Muscular Dystrophy
Location: New York NY
Sponsor: Benitec Biopharma, Inc.

Sex: All

Age: 0 - 65

Code: NCT06185673

Phase 1, Phase 2, Recruiting

Investigating Exercise in Myotonic Dystrophy Type 2 (DM2)

for
Myotonic Dystrophy 2
Location: Boston MA
Sponsor: Massachusetts General Hospital

Sex: All

Age: 18 - 70

Code: NCT06716931

Recruiting

Investigational Use of Neuromuscular Ultrasound

for
Muscular Dystrophy, Peripheral Neuropathy,
Location: Bethesda MD
Sponsor: National Institute of Neurological Disorders and Stroke (NINDS)

Sex: All

Age: 18 - 70+

Code: NCT05237973

Recruiting

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A Study About the Safety of a Single ASP2020 Eye Injection and if it Helps People With Vision Loss From Stargardt-type Eye Conditions

for
Stargardt Disease, Stargardt Macular Dystrophy,
Location: Cincinnati OH, Dallas TX, Phoenix AZ
Sponsor: Astellas Institute for Regenerative Medicine

Sex: All

Age: 6+

Code: NCT07734064

Phase 1, Recruiting

Brain Stimulation Effects on Orientation and Mobility Skills in Adults With Vision Impairment

for
Retinitis Pigmentosa (RP), Rod Cone Dystrophy,
Location: Waterloo
Sponsor: University of Waterloo

Sex: All

Age: 18+

Code: NCT07341763

Recruiting

Remote Assessments and Genetic Determinants of Congenital and Childhood Myotonic Dystrophy

for
Myotonic Dystrophy Type 1, Congenital DM1, Juvenile DM1,
Location: Rochester NY
Sponsor: University of Rochester

Sex: All

Age: 0 - 17

Code: NCT07630389

Recruiting

PBGENE-DMD Phase 1/2a Safety and Preliminary Efficacy Study in Duchenne Muscular Dystrophy (FUNCTION-DMD)

for
Duchenne Muscular Dystrophy With Mutations Amenable to PBGENE-DMD,
Location: St Louis MO, Little Rock AR
Sponsor: Precision BioSciences, Inc.

Sex: Male

Age: 2 - 7

Code: NCT07429240

Phase 1, Phase 2, Recruiting

Muscle Health Measurements Using Electrical Impedance Myography

for
Myopathy, Muscular Dystrophies, Myositis, Myofibrillar Myopathy,
Location: Boston MA
Sponsor: Beth Israel Deaconess Medical Center

Sex: All

Age: 18 - 70+

Code: NCT07502989

Recruiting

A Phase 1/2 Study to Assess the Safety, Tolerability, Pharmacokinetics, and Pharmacodynamics of BMN 351 in Participants With Duchenne Muscular Dystrophy

for
Duchenne Muscular Dystrophy
Location: London
Sponsor: BioMarin Pharmaceutical

Sex: Male

Age: 4 - 10

Code: NCT06280209

Phase 1, Phase 2, Recruiting

Effects of Whole-body Electrical Muscle Stimulation Exercise on Adults With Neuromuscular Disease

for
Neuromuscular Diseases (NMD), Amyotrophic Lateral Sclerosis,
Location: Columbia MO
Sponsor: University of Missouri-Columbia

Sex: All

Age: 18+

Code: NCT07478172

Recruiting

A Study to Learn How Stargardt-type Eye Conditions Progress in Children and Adults

for
Stargardt Disease, Stargardt Macular Dystrophy,
Location: Philadelphia PA, Durham NC, Miami FL, Pittsburgh PA,
Sponsor: Astellas Pharma Global Development, Inc.

Sex: All

Age: 6+

Code: NCT07425574

Recruiting

BetterLife FSHD: A Patient-driven Health and Research Platform

for
FSH, FSH Muscular Dystrophy,
Location: Randolph MA
Sponsor: FSHD Society

Sex: All

Age: 1+

Code: NCT07409142

Recruiting

A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP-9001) in Participants With Duchenne Muscular Dystrophy (DMD) - Non-Ambulatory Cohort

for
Duchenne Muscular Dystrophy
Location: Norfolk VA, Durham NC, Gainesville FL, Chicago IL,
Sponsor: Sarepta Therapeutics, Inc.

Sex: Male

Age: 2+

Code: NCT04626674

Phase 1, Recruiting

Randomized Stepped Wedge Study of Emapalumab in APECED Enteritis

for
Autoimmune Polyendocrinopathy Candidiasis Ectodermal Dystrophy Enteritis,
Location: Bethesda MD
Sponsor: National Institute of Allergy and Infectious Diseases (NIAID)

Sex: All

Age: 2 - 70+

Code: NCT07202598

Phase 2, Recruiting

Cerebrospinal Fluid Biomarkers of Myotonic Dystrophy

for
Myotonic Dystrophy Type 1
Location: Boston MA
Sponsor: Massachusetts General Hospital

Sex: All

Age: 18+

Code: NCT06075693

Recruiting

A Study Evaluating the Real-World Experience of Givinostat in Patients With Duchenne Muscular Dystrophy

for
Duchene Muscular Dystrophy
Location: Boston MA, Worcester MA, New York NY,
Sponsor: ITF Therapeutics LLC

Sex: All

Age: 6+

Code: NCT07127978

Recruiting

Establishing Biomarkers and Clinical Endpoints in Myotonic Dystrophy Type 1 (END-DM1) Extension

for
DM1, Myotonic Dystrophy, Myotonic Dystrophy 1,
Location: Richmond VA
Sponsor: Virginia Commonwealth University

Sex: All

Age: 18 - 70

Code: NCT07700225

Recruiting

Modeling Mortality in Duchenne Muscular Dystrophy Cardiomyopathy: Identification of Surrogate Outcome Measures for DMD Drug Trials

for
Duchenne Muscular Dystrophy (DMD), Cardiomyopathy,
Location: Washington D.C. DC, Richmond VA, Durham NC, Columbus OH,
Sponsor: Vanderbilt University Medical Center

Sex: All

Age: 0+

Code: NCT07674758

Recruiting