Location: Boston MA, Washington D.C. DC, Columbus OH,
Sponsor: Alexion Pharmaceuticals, Inc.
Sex: All
Age: 18+
Code: NCT05966467
Recruiting
A Natural History Study Seeks to Understand the Clinical, Genomic, Pharmacological, Laboratory, and Dietary Determinates of Pyrimidine and Purine Metabolism Disorders
for
AMPD3, OMIM*102772, AMP Deaminase Deficiency,
Location: Bethesda MD
Sponsor: National Human Genome Research Institute (NHGRI)
Sex: All
Age: 0 - 70+
Code: NCT06092346
Recruiting
Non-interventional Study of Patients With Transthyretin (ATTR) Amyloidosis
Proof of Concept Trial of Cannabis Derivatives in Neuropathic Pain
for
Neuropathic Pain, Peripheral Neuropathic Pain
Location: Providence RI, West Haven CT, San Antonio TX,
Sponsor: VA Office of Research and Development
Sex: All
Age: 21+
Code: NCT05351801
Phase2, Recruiting
Detection of Vocal Fold Motion Impairment on Noninvasive Positive Pressure
for
Vocal Cord Dysfunction, Vocal Cord Paralysis,
Location: Queens NY
Sponsor: Nemours Children's Clinic
Sex: All
Age: 0 - 18
Code: NCT06406725
Recruiting
A Worldwide Pregnancy Safety Study to Assess Maternal, Fetal, and Infant Outcomes Following Exposure to Efgartigimod During Pregnancy and/or Breastfeeding.
for
Myasthenia Gravis,
Location: Morgantown WV
Sponsor: argenx
Sex: Female
Age: 0+
Code: NCT06299748
Recruiting
Evaluation of Efficacy and Safety of VX-993 for Pain Associated With Diabetic Peripheral Neuropathy
for
Diabetic Peripheral Neuropathic Pain
Location: Montreal, Toronto, Brampton, Kelowna
Sponsor: Vertex Pharmaceuticals Incorporated
Sex: All
Age: 18 - 70+
Code: NCT06619860
Phase2, Recruiting
An Open Label Clinical Study to Evaluate Tanruprubart (Also Commonly Known as ANX005) in Participants With Guillain-Barré Syndrome (FORWARD Study)
for
Guillain-Barre Syndrome
Location: Worcester MA, Jacksonville FL, Detroit MI, Rochester MN,