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Prospective Clinical Assessment Study in Children With Hypochondroplasia
for
Hypochondroplasia
Location: Cincinnati OH, London, Nashville TN, Madison WI,
Sponsor: QED Therapeutics, a BridgeBio company
Sex: All
Age: 2 - 16
Code: NCT06410976
Recruiting
A Real-world Long-term Safety and Immunogenicity Study of Olipudase Alfa Therapy in Pediatric Patients Less Than 2 Years of Age With Acid Sphingomyelinase Deficiency (ASMD)